Keya Hatkar, a young author and motivational speaker with Spinal Muscular Atrophy, inspires others with her resilience and ...

Haris Beeran urges government intervention to make affordable SMA medicines available in India, addressing the high costs and patent issues.

Upper House member Haris Beeran has said the current costs of medicines approved for SMA are 'beyond the reach of the central ...

Novartis has recently announced that its intrathecal (IT) formulation of onasemnogene abeparvovec (OAV101 IT) successfully ...

Novartis has recently announced that its intrathecal (IT) formulation of onasemnogene abeparvovec (OAV101 IT) successfully achieved the primary endpoint in a Phase III STEER study (NCT05089656) ...

US FDA grants orphan drug designation to NMD Pharma’s NMD670 to treat patients with Charcot-Marie-tooth disease: Aarhus, Denmark Tuesday, January 7, 2025, 16:00 Hrs [IST] NMD Ph ...

Bernstein has upgraded Beam Therapeutics (NASDAQ:BEAM) to outperform from market perform, citing upcoming data on the company ...

A new electrically active transplantable material that can help to regrow cells in the brain and spinal cord could redefine ...

The FDA has approved a first-of-its-kind treatment for dry age-related macular degeneration (AMD), a leading cause of blindness in adults over 55.

A New York appellate court on Tuesday denied President-elect Donald Trump's bid to halt sentencing set for Friday for his conviction on criminal charges stemming from hush money paid to a porn ...

An Emboldened Trump Talks of Taking Greenland and Panama Canal by Force In a rambling news conference from his private Florida club, President-elect Trump refused to rule out using military force ...

A team at the University of Calgary is making scientific advances in understanding plant adaptation, which could ultimately be used to find ways to make agricultural crops more resilient to heat ...